![]() | Up a level |
König, Kirsten; Pechmann, Astrid; Thiele, Simone; Walter, Maggie C.; Schorling, David; Tassoni, Adrian; Lochmüller, Hanns; Müller-Reible, Clemens; Kirschner, Janbernd (2019): De-duplicating patient records from three independent data sources reveals the incidence of rare neuromuscular disorders in Germany. In: Orphanet Journal of Rare Diseases, Vol. 14, 152
Pechmann, Astrid; König, Kirsten; Bernert, Guenther; Schachtrup, Kristina; Schara, Ulrike; Schorling, David; Schwersenz, Inge; Stein, Sabine; Tassoni, Adrian; Vogt, Sibylle; Walter, Maggie C.; Lochmüller, Hanns; Kirschner, Janbernd (2019): SMArtCARE - A platform to collect real-life outcome data of patients with spinal muscular atrophy. In: Orphanet Journal of Rare Diseases, Vol. 14, 18