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Anzahl der Publikationen: 6
Zeitschriftenartikel
Carelli, Valerio; Newman, Nancy J.; Yu-Wai-Man, Patrick; Biousse, Valerie; Moster, Mark L.; Subramanian, Prem S.; Vignal-Clermont, Catherine; Wang, An-Guor; Donahue, Sean P.; Leroy, Bart P.; Sergott, Robert C.; Klopstock, Thomas; Sadun, Alfredo A.; Fernandez, Gema Rebolleda; Chwalisz, Bart K.; Banik, Rudrani; Girmens, Jean Francois; La Morgia, Chiara; DeBusk, Adam A.; Jurkute, Neringa; Priglinger, Claudia; Karanjia, Rustum; Josse, Constant; Salzmann, Julie; Montestruc, Francois; Roux, Michel; Taiel, Magali; Sahel, Jose-Alain und Group, The Lhon Study
(2022):
Indirect Comparison of Lenadogene Nolparvovec Gene Therapy Versus Natural History in Patients with Leber Hereditary Optic Neuropathy Carrying the m.11778G > A MT-ND4 Mutation.
In: Ophthalmology and Therapy, Bd. 12, Nr. 1: S. 401-429
Newman, Nancy J.; Yu-Wai-Man, Patrick; Carelli, Valerio; Biousse, Valerie; Moster, Mark L.; Vignal-Clermont, Catherine; Sergott, Robert C.; Klopstock, Thomas; Sadun, Alfredo A.; Girmens, Jean-Francois; La Morgia, Chiara; DeBusk, Adam A.; Jurkute, Neringa; Priglinger, Claudia; Karanjia, Rustum; Josse, Constant; Salzmann, Julie; Montestruc, Francois; Roux, Michel; Taiel, Magali und Sahel, Jose-Alain
(24. Mai 2021):
Intravitreal Gene Therapy vs. Natural History in Patients With Leber Hereditary Optic Neuropathy Carrying the m.11778G>A ND4 Mutation: Systematic Review and Indirect Comparison.
In: Frontiers in Neurology, Bd. 12, 662838
[PDF, 592kB]
Moster, Mark L.; Sergott, Robert C.; Newman, Nancy J.; Yu-Wai-Man, Patrick; Carelli, Valerio; Bryan, Molly Scannell; Smits, Gerard; Biousse, Valerie; Vignal-Clermont, Catherine; Klopstock, Thomas; Sadun, Alfredo A.; DeBusk, Adam A.; Carbonelli, Michele; Hage, Rabih; Priglinger, Siegfried; Karanjia, Rustum; Blouin, Laure; Taiel, Magali; Katz, Barrett und Sahel, Jose Alain
(2021):
Cross-Sectional Analysis of Baseline Visual Parameters in Subjects Recruited Into the RESCUE and REVERSE ND4-LHON Gene Therapy Studies.
In: Journal of Neuro-Ophthalmology, Bd. 41, Nr. 3: S. 298-308
Newman, Nancy J.; Yu-Wai-Man, Patrick; Carelli, Valerio; Moster, Mark L.; Biousse, Valerie; Vignal-Clermont, Catherine; Sergott, Robert C.; Klopstock, Thomas; Sadun, Alfredo A.; Barboni, Piero; DeBusk, Adam A.; Girmens, Jean Francois; Rudolph, Guenther; Karanjia, Rustum; Taiel, Magali; Blouin, Laure; Smits, Gerard; Katz, Barrett und Sahel, Jose-Alain
(2021):
Efficacy and Safety of Intravitreal Gene Therapy for Leber Hereditary Optic Neuropathy Treated within 6 Months of Disease Onset.
In: Ophthalmology, Bd. 128, Nr. 5: S. 649-660
Catarino, Claudia B.; Livonius, Bettina von; Priglinger, Claudia; Banik, Rudrani; Matloob, Selma; Tamhankar, Madhura A.; Castillo, Lorena; Friedburg, Christoph; Halfpenny, Christopher A.; Lincoln, John A.; Traber, Ghislaine L.; Acaroglu, Goelge; Black, Graeme C. M.; Doncel, Carlos; Fraser, Clare L.; Jakubaszko, Joanna; Landau, Klara; Langenegger, Stefan J.; Munoz-Negrete, Francisco J.; Newman, Nancy J.; Poulton, Joanna; Scoppettuolo, Elisabetta; Subramanian, Prem; Toosy, Ahmed T.; Vidal, Mariona; Vincent, Andrea L.; Votruba, Marcela; Zarowski, Marcin; Zermansky, Adam; Lob, Felice; Rudolph, Guenther; Mikazans, Oskars; Silva, Magda; Lloria, Xavier; Metz, Guenther und Klopstock, Thomas
(2020):
Real-World Clinical Experience With Idebenone in the Treatment of Leber Hereditary Optic Neuropathy.
In: Journal of Neuro-Ophthalmology, Bd. 40, Nr. 4: S. 558-565
Yu-Wai-Man, Patrick; Newman, Nancy J.; Carelli, Valerio; Moster, Mark L.; Biousse, Valerie; Sadun, Alfredo A.; Klopstock, Thomas; Vignal-Clermont, Catherine; Sergott, Robert C.; Rudolph, Gunther; La Morgia, Chiara; Karanjia, Rustum; Taiel, Magali; Blouin, Laure; Burguiere, Pierre; Smits, Gerard; Chevalier, Caroline; Masonson, Harvey; Salermo, Yordak; Katz, Barrett; Picaud, Serge; Calkins, David J. und Sahel, Jose-Alain
(2020):
Bilateral visual improvement with unilateral gene therapy injection for Leber hereditary optic neuropathy.
In: Science Translational Medicine, Bd. 12, Nr. 573, eaaz7423