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Bremova-Ertl, Tatiana; Platt, Frances; Strupp, Michael (2020): Sandhoff Disease: Improvement of Gait by Acetyl-DL-Leucine: A Case Report. In: Neuropediatrics, Vol. 51, No. 06: pp. 450-452
Platt, Frances; Strupp, Michael (2016): An anecdotal report by an Oxford basic neuroscientist: effects of acetyl-DL-leucine on cognitive function and mobility in the elderly. In: Journal of Neurology, Vol. 263, No. 6: pp. 1239-1240