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Pechmann, Astrid; König, Kirsten; Bernert, Guenther; Schachtrup, Kristina; Schara, Ulrike; Schorling, David; Schwersenz, Inge; Stein, Sabine; Tassoni, Adrian; Vogt, Sibylle; Walter, Maggie C.; Lochmüller, Hanns; Kirschner, Janbernd (2019): SMArtCARE - A platform to collect real-life outcome data of patients with spinal muscular atrophy. In: Orphanet Journal of Rare Diseases, Vol. 14, 18